Selection from HEOR Bibliography

IMS logo
Search criteria
Condition: Rare Diseases
 
CO71 Investigating the Secondary Care System Burden of Glycogen Storage Disease Type IA (GSDIA) Using the HES Database
Authors: E Kruger S Chavda RN Gupta V Valayannopoulos
Affiliations: Ultragenyx Pharmaceutical Inc., Novato, CA, USA IQVIA, London, UK Ultragenyx Pharmaceutical Inc., Cambridge, MA, USA
Publications: 
Kruger, E et al. Value in Health, Volume 25, Issue 7, S317
Document Types: , Abstract, Article
Countries: , England
Abstract: https://www.valueinhealthjournal.com/article/S1098-3015(22)00370-9/pdf#%20
Condition Year Language Analysis type
, Metabolic Disorders , Rare disease, Rare Diseases 2022 English , Burden of illness, clinical setting: Secondary care, Quality of life
 
 
Demographic characteristics, thromboembolism risk, and treatment patterns for patients with cold agglutinin disease in Japan
Authors: Toyomi Kamesaki 1, Jun-Ichi Nishimura 2, Hideho Wada 3, Eric Yu 4, Elisa Tsao 5, Jaime Morales 5, Yuzuru Kanakura 2 6 (rwesheorj 4)
Affiliations: 1) Division of Support in Community Medicine, Center for Community Medicine, Regional Medical Center, Center for Regional Medical Care, Jichi Medical University, 3311 - 1 Yakushiji Shimotsuke-shi, Tochigi, Japan 2) Osaka University, Osaka, Japan 3) Kawasaki Medical School, Kurashiki, Japan 4) IQVIA Solutions K.K., Tokyo, Japan 5) Sanofi, Waltham, MA, USA 6) Sumitomo Hospital, Osaka, Japan
Publications: 
International Journal of Hematology
Document Types: , Article
Countries: , Japan
Abstract: https://link.springer.com/article/10.1007%2Fs12185-020-02899-6
Condition Year Language Analysis type
, Rare Diseases 2020 English , Retrospective database analysis
 
 
Evidence synthesis in pulmonary arterial hypertension: a systematic review and critical appraisal
Authors: Max Schlueter, Amélie Beaudet, Evan Davies, Binu Gurung, Andreas Karabis
Affiliations: IQVIA, 210 Pentonville Road, London, N1 9JY; IQVIA, Herikerbergweg 314, 1101 CT, Amsterdam, Netherlands; Department of Statistical Science, University College London, London, WC1E 6BT, UK.
Publications: 
Document Types: , Article
Countries: 
Abstract: https://bmcpulmmed.biomedcentral.com/articles/10.1186/s12890-020-01241-4
Condition Year Language Analysis type
, Comparative Effectiveness & Health Technology Assessment, Methodology, Rare Diseases 2020 English , Literature Review, Review
 
 
A network meta analysis comparing C1 and kallikrein inhibitors approved for prophylaxis of hereditary angioedema in the United States
Authors: P. Saharia1, P. Soni2, M. Chatterjee3
Affiliations: IQVIA, Gurugram, HR, India; IQVIA, Delhi, India; IQVIA, Gurugram, India
Publications: 
DOI: https://doi.org/10.1016/j.jval.2019.04.1641
Document Types: , Article
Countries: , USA
Abstract: https://www.valueinhealthjournal.com/article/S1098-3015(19)31833-9/fulltext
Condition Year Language Analysis type
, Cardiovascular disease, Rare Diseases 2019 English , Literature Review, Meta analysis
 
 
Identification of a hereditary angioedema cohort in a US ambulatory EMR database
Authors: Brouwer E, Bratton E, Near A, Lang K, Mack C
Affiliations: 
Publications: 
Pharmacoepidemiol Drug Saf 2018; 27 (2): 136-137.
Document Types: , Poster
Countries: 
Condition Year Language Analysis type
, Rare Diseases 2018 English
 
 
Rare disease development programs: An update
Authors: Wu J, Want C, Horton DB, Petersen I, Oliveria S, Blackburn S, Jiang J, LoCasale R.
Affiliations: 
Publications: 
Pharmacoepidemiol Drug Saf 2018; 27 (2):5.
Document Types: , Poster
Countries: 
Condition Year Language Analysis type
, Rare Diseases 2018 English
 
 
WHAT INTERPRETATION OF ICERS IN ORPHAN DISEASES? A FRENCH EXAMPLE.
Authors: Moutier Hélène; Bourguignon Sandrine; Maurel Frédérique; Bodaghi Charles
Affiliations: RWI IQVIA France
Publications: 
ISPOR 2018
Document Types: , Poster
Countries: , France
Condition Year Language Analysis type
, Comparative Effectiveness & Health Technology Assessment, Health economics, Pricing and reimbursement, Rare Diseases 2018 English , Cost effectiveness, Pricing & Reimbursement, Willingness to pay
 
 
Healthcare resource utilization and costs associated with long-term corticosteroid exposure in patients with systemic lupus erythematosus
Authors: Kabadi S, Yeaw J, Bacani AK, Tafesse E, Bos K, Karkare S, DeKoven M, Vina ER
Affiliations: AstraZeneca, IQVIA
Publications: 
Lupus
Document Types: , Article
Countries: , USA
Abstract: http://journals.sagepub.com/doi/abs/10.1177/0961203318790675?url_ver=Z39.88-2003&rfr_id=ori%3Arid%3Acrossref.org&rfr_dat=cr_pub%3Dpubmed&
Condition Year Language Analysis type
, Rare Diseases 2018 English , Cost analysis, Retrospective cohort analysis
 
 
Health Care Resource Utilization Among a US Cohort Treated for Hereditary Angioedema, 2010–2015
Authors: Tachdjian R, Johnson KE, Casso D, Oliveria SA, Devercelli G, Jain G.
Affiliations: Tachdjian R: UCLA School of Medicine; Johnson KE: IQVIA (formerly); Casso D: IQVIA; Oliveria SA: IQVIA; Devercelli G: Shire; Jain G: Shire
Publications: 
2018 American Academy of Allergy, Asthma and Immunology (AAAAI)/World Allergy Organization (WAO) Joint Congress
Document Types: , Poster
Countries: , USA
Condition Year Language Analysis type
, Patient Registries & Real-World Study Methods, Rare Diseases 2018 English , Cost analysis, Database Study, Epidemiological study, Retrospective database analysis
 
 
Demographic Characteristics and Treatment Patterns among Patients Treated for Hereditary Angioedema in a U.S. Cohort, 2006-2015
Authors: Tachdjian R, Johnson KE, Casso D, Oliveria SA, Devercelli G, Jain G
Affiliations: Tachdjian R: UCLA School of Medicine (Department of Medicine and Pediatrics), Johnson KE: IQVIA (formerly); Casso D: IQVIA; Oliveria SA: IQVIA; Devercelli G: Shire; Jain G: Shire.
Publications: 
34th International Conference on Pharmacoepidemiology & Therapeutic Risk Management
Document Types: , Abstract
Countries: , USA
Condition Year Language Analysis type
, Rare Diseases 2018 English , Database Study, Epidemiological study, Retrospective cohort analysis, Retrospective database analysis
 
 
High levels of healthcare utilization prior to diagnosis in idiopathic pulmonary arterial hypertension support the feasibility of an early diagnosis algorithm: the SPHInX project
Authors: Rito Bergemann, James Allsopp, Harvey Jenner, Flora Ashley Daniels, Edmund Drage, Yevgeniy Samyshkin, Claude Schmitt, Steven Wood, David G. Kiely, Allan Lawrie
Affiliations: "1GlaxoSmithKline, Brentford, Middlesex, UK 2Current affiliation: Evalueserve Life Sciences Healthcare, London, UK 3Scientific Computing Group, Sheffield Teaching Hospitals Foundation Trust, Sheffield, UK 4IQVIA, London, UK 5Department of Infection, Immunity & Cardiovascular Disease, University of Sheffield, Sheffield, UK 6National Pulmonary Hypertension Service (Sheffield), Sheffield Pulmonary Vascular Unit, Royal Hallamshire Hospital, Sheffield, UK 7INSIGNEO, University of Sheffield, Sheffield, UK"
Publications: 
Pulm Circ. 2018 Oct-Dec;8(4):2045894018798613. doi: 10.1177/2045894018798613.
Document Types: , Article
Countries: , UK
Condition Year Language Analysis type
, Cardiovascular disease, Database Validity and methodology, Rare Diseases, Respiratory disease 2018 English , Retrospective database analysis
 
 
Real world data from hospital episode statistics can be used to determine patients at risk of idiopathic pulmonary arterial hypertension
Authors: "David G. Kiely MD, Allan Lawrie, Orla Doyle PhD, Valentina Salvatelli PhD, Flora Ashley Daniels PhD, Edmund Drage, Harvey Jenner, John Rigg, Claude Schmitt, Yevgeniy Samyshkin, Rito Bergemann "
Affiliations: 1Sheffield Pulmonary Vascular Disease Unit, Royal Hallamshire Hospital, Sheffield Teaching Hospitals NHS Foundation Trust, Glossop Road, Sheffield, UK; 2Real-World & Analytical Solutions, IQVIA, London, UK; 3GSK, Brentford, Middlesex, UK; 4Department of Infection, Immunity & Cardiovascular Disease, University of Sheffield, Sheffield, UK; 5INSIGNEO, University of Sheffield, Sheffield, UK; 6Evalueserve UK Ltd, London, UK. 1 Sheffield Pulmonary Vascular Disease Unit, Royal Hallamshire Hospital, Sheffield Teaching Hospitals NHS Foundation Trust, Glossop Road, Sheffield, UK. 2 Department of Infection, Immunity & Cardiovascular Disease, University of Sheffield, Sheffield, UK. 3 INSIGNEO, University of Sheffield, Sheffield, UK. 4 Real-World & Analytical Solutions, IQVIA, London, UK. 5 GlaxoSmithKline, Brentford, Middlesex, UK.
Publications: 
European Respiratory Journal 2018 52: Suppl. 62, PA3082.
Document Types: , Poster
Countries: , UK
Condition Year Language Analysis type
, Cardiovascular disease, Database Validity and methodology, Rare Diseases, Respiratory disease 2018 English , Retrospective database analysis
 
 
Studies on economic burden of disease using real-world healthcare data in Japan: a systematic review
Authors: WY Kuan 1, Sven Demiya 1, Eric Yu 1, Y Piao 1 (rwesheorj 1)
Affiliations: 1) IQVIA Solutions Japan K.K., Tokyo, Japan
Publications: 
ISPOR Asia Pacific 2018 Conference
Document Types: , Abstract
Countries: , Japan
Abstract: https://www.ispor.org/heor-resources/presentations-database/presentation/ispor-asia-pacific-2018/studies-on-economic-burden-of-disease-using-real-world-healthcare-data-in-japan-a-systematic-review
Condition Year Language Analysis type
, Rare Diseases 2018 English , Economic evaluation, Literature Review
 
 
Unspecified intestinal malabsorption in patients treated with angiotensin-converting enzyme inhibitors or angiotensin receptor blockers: a retrospective analysis in primary care settings
Authors: De Bortoli N1, Ripellino C2, Cataldo N3, Marchi S1
Affiliations: 1 Gastroenterology Unit, Department of Translational Research and New Technologies in Medicine and Surgery, University of Pisa, Pisa, Italy 2 Department of Real World Evidence, HEOR Consultant Freelance, Milan, Italy 3 Department of Real World Evidence, QuintilesIMS, Milan, Italy
Publications: 
Expert Opinion on Drug Safety. doi: 10.1080/14740338.2017.1376647. [Epub ahead of print]
Document Types: , Article
Countries: , Germany, Italy
Abstract: https://www.ncbi.nlm.nih.gov/pubmed/28871813
Condition Year Language Analysis type
, Drug safety, Gastrointestinal disorders, Rare Diseases 2017 English , Clinical setting: Primary care, Database Study, Real World Data, Real World Evidence, Retrospective cohort analysis, Retrospective database analysis
 
 
CLOSING THE EVIDENCE GAP FOR ORPHAN DRUGS: DO GERMAN REGULATORY REQUIREMENTS GIVE INCENTIVES FOR HIGH LEVEL EVIDENCE GENERATION?
Authors: Ana Babac, Roger-Axel Greiner, Doreen Bonduelle
Affiliations: "QuintilesIMS, IMS Health GmbH & Co. OHG, Landshuter Allee 10, 80637 München "
Publications: 
ISPOR 20th Annual European Congress, Glasgow
Document Types: , Poster
Countries: , Germany
Abstract: https://www.ispor.org/Event/ProgramList/2017Glasgow?type=Poster&sess=II&acode=PHS
Condition Year Language Analysis type
, Rare Diseases 2017 English , Pricing & Reimbursement, Retrospective database analysis
 
 
Creating a Rare Disease Cohort Using Ambulatory Electronic Medical Record (AEMR) Data: Duchenne Muscular Dystrophy (DMD)
Authors: Anderson A1, Casso D1, Susan A. Oliveria SA 1, Douglas Kou T 2
Affiliations:  1 QuintilesIMS ,2 BMS
Publications: 
33rd International Conference on Pharmacoepidemiology & Thereputic Risk Management; August, 28, 2017; Montreal, Canada
Document Types: , Poster
Countries: , USA
Condition Year Language Analysis type
, Database Validity and methodology, Musculoskeletal disease, Patient Registries & Real-World Study Methods, Rare Diseases 2017 English , Epidemiological study, Observational study, Retrospective cohort analysis, Retrospective database analysis
 
 
Creating a Rare Disease Cohort Using Ambulatory Electronic Medical Record Data: Progressive Supranuclear Palsy
Authors: Anderson A, Casso D, Oliveria SA, Kou TD
Affiliations: AA, DC, and SAO are employees of QuintilesIMS. TDK is an employee of BMS
Publications: 
33rd International Conference on Pharmacoepidemiology and Therapeutic Risk Management, August 26-30, 2017; Montreal, Canada
Document Types: , Poster
Countries: , USA
Condition Year Language Analysis type
, Neurological disorders, Patient Registries & Real-World Study Methods, Rare Diseases 2017 English , Epidemiological study, Retrospective cohort analysis
 
 
Demographic Characteristics and Treatment Patterns Among Patients Treated for Hereditary Angioedema in a US Cohort, 2006-2015
Authors: Raffi Tachdjian, Karin E. Johnson, Deborah Casso1, Susan A. Oliveria1, Giovanna Devercelli2, Gagan Jain2
Affiliations: 1, QuintilesIMS ; 2, Shire Development LLC
Publications: 
North American Rhinology & Allergy Conference, February 9–11, 2017, Puerto Rico
Document Types: , Poster
Countries: , USA
Condition Year Language Analysis type
, Patient Registries & Real-World Study Methods, Rare Diseases 2017 English , Epidemiological study, Retrospective cohort analysis
 
 
Demographic Characteristics and Treatment Patterns Among Patients Treated for Hereditary Angioedema in a US Cohort, 2006–2015
Authors: Tachdjian R, Johnson KE, Casso D, Oliveria SA, Devercelli G, Jain G
Affiliations: Tachdjian R, Johnson KE, Casso D, Oliveria SA, Devercelli G, Jain G Tachdjian R: UCLA School of Medicine; Johnson KE: IQVIA (formerly); Casso D: IQVIA; Oliveria SA: IQVIA; Devercelli G: Shire; Jain G: Shire
Publications: 
North American Rhinology & Allergy Conference: Puerto Rico
Document Types: , Abstract
Countries: , USA
Condition Year Language Analysis type
, Rare Diseases 2017 English , Database Study, Epidemiological study, Retrospective cohort analysis, Retrospective database analysis
 
 
Orphan Drug Expenditures In The United States: A Historical And Prospective Analysis, 2007-18.
Authors: Divino V1, DeKoven M2, Kleinrock M3, Wade RL4, Kaura S5.
Affiliations: 1 Victoria Divino (vdivino@us.imshealth.com) is a senior consultant at IMS Health in Fairfax, Virginia. 2 Mitch DeKoven is a principal at IMS Health. 3 Michael Kleinrock is director of research development for the IMS Institute for Healthcare Informatics, in Parsippany, New Jersey. 4 Rolin L. Wade is a senior principal at IMS Health. 5 Satyin Kaura is a senior director at Celgene Corporation, in Summit, New Jersey.
Publications: 
Health Aff (Millwood). 2016 Sep 1;35(9):1588-94
Document Types: , Article
Countries: , USA
Condition Year Language Analysis type
, Rare Diseases 2016 English , Budget impact
 
 
Pharmaceutical expenditure on drugs for rare diseases in Canada: a historical (2007-13) and prospective (2014-18) MIDAS sales data analysis.
Authors: Divino V1, DeKoven M2, Kleinrock M3, Wade RL2, Kim T4, Kaura S5.
Affiliations: 1 IMS Health, 8280 Willow Oaks Corporate Drive, Suite 775, Fairfax, VA, 22031, USA. vdivino@us.imshealth.com. 2 IMS Health, 8280 Willow Oaks Corporate Drive, Suite 775, Fairfax, VA, 22031, USA. 3 IMS Institute for Healthcare Informatics, One IMS Drive, Plymouth Meeting, PA, 19462, USA. 4 Celgene, 6755 Mississauga Rd, Suite 600, Mississauga, ON, L5N 7Y2, Canada. 5 Celgene, 86 Morris Avenue, H-222H, Summit, NJ, 07901, USA.
Publications: 
Orphanet J Rare Dis. 2016 May 21;11(1):68
Document Types: , Article
Countries: , Canada
Abstract: https://www.ncbi.nlm.nih.gov/pmc/articles/PMC4875716/
Condition Year Language Analysis type
, Rare Diseases 2016 English , Budget impact
 
 
Copyright © 2024 IMS Health Incorporated. All rights reserved.